Biography:
Beth Zanrucha, PharmD, has more than a decade of Medical Affairs experience and over 15 years in pharmacy practice, spanning rare neurogenetic, neuromuscular, and lysosomal disease at Sarepta Therapeutics and IntraBio Inc. During her career she has built Medical Affairs capabilities across medical information, medical managed care, field medical, and global medical strategy, supporting first-in-disease and first-in-class launches in the United States and Europe. She has served as team lead for a gene therapy development program, delivered clinical and health economic evidence to national payers and state Medicaid boards, and established thought leader and advisory board programs globally. Currently, she is serving as Senior Medical Director, Global Medical Affairs at IntraBio Inc., a biopharmaceutical company developing therapies for rare and orphan neurological and neurodegenerative diseases, where she leads global medical strategy across Niemann-Pick disease type C, ataxia-telangiectasia, GM2 gangliosidosis, and CACNA1A-related disorders.


Title : Results from the global phase 3 trial (IB1001-303) evaluating levacetylleucine in children and adults with ataxia-telangiectasia
Title : A phase 3, multinational, randomized, placebo-controlled, double-blind, crossover trial (IB1001-304) evaluating levacetylleucine in CACNA1A